Gene editing emerges as a new therapeutic strategy for Duchenne muscular dystrophy
Advances in gene editing technology have spurred considerable progress towards a treatment for Duchenne muscular dystrophy (DMD). Although the disease is rare – affecting roughly 1 in 5,000 male births – its consequences are devastating: patients are confined to wheelchairs at an early age and often succumb to heart or respiratory failure in their twenties or thirties. No treatments are currently available, but three separate … Continue reading Gene editing emerges as a new therapeutic strategy for Duchenne muscular dystrophy